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- Gene editing of DNAH11 restores normal cilia motility in primary ciliary dyskinesiaMichele Lai, Massimo Pifferi, Andrew Bush, Martina Piras, Angela Michelucci, Maria Di Cicco, Ambra del Grosso, Paola Quaranta, Chiara Cursi, Elena Tantillo, Sara Franceschi, Maria Chiara Mazzanti, Paolo Simi, Giuseppe Saggese, Attilio Boner, Mauro PistelloJournal of Medical Genetics Apr 2016, 53 (4) 242-249; DOI: 10.1136/jmedgenet-2015-103539
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